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Next type of congenital hearing loss gene therapy study results published by end of 2025
5
Resolution / Starting Odds
DFNB1 • 50%
DFNB4 • 25%
DFNB7/11 • 25%
Publication in peer-reviewed medical journals
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Gene Therapy in China Restores Hearing in Five Deaf Children
Jun 5, 2024, 09:20 AM
A pioneering gene therapy trial in China has successfully restored hearing in both ears of children who were born deaf. The trial, which involved five children, provided a normal copy of a mutated gene, specifically targeting a condition called DFNB9 caused by Otof mutations. This condition accounts for 2-8% of all congenital hearing loss. As a result of the therapy, the children can now listen and dance to music. The study was published in Nature Medicine and The Lancet.
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