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Follow-up study on long-term effects of DFNB9 gene therapy published by mid-2025?
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Resolution / Starting Odds
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Publication in a peer-reviewed medical journal
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Gene Therapy in China Restores Hearing in Five Deaf Children
Jun 5, 2024, 09:20 AM
A pioneering gene therapy trial in China has successfully restored hearing in both ears of children who were born deaf. The trial, which involved five children, provided a normal copy of a mutated gene, specifically targeting a condition called DFNB9 caused by Otof mutations. This condition accounts for 2-8% of all congenital hearing loss. As a result of the therapy, the children can now listen and dance to music. The study was published in Nature Medicine and The Lancet.
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Success • 33%
Partial Success • 33%
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Successful phase 3 trial by another company • 25%
New regulatory approval • 25%
Major partnership or acquisition • 25%
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